Comments for Muscular Dystrophy News – The Web's Daily Resource for Muscular Dystrophy News

Comment on Stable heart health seen long-term for women with BMD, �鶹�� mutations by Adriel Hernando

Adriel Hernando — Wed, 08 Jul 2026 14:41:49 +0000

Very cool article, but also important to emphasize that symptomatic female carriers for �鶹�� represent 10-20% of the female population. And skewed X chromosome inactivation is the main cause of female carriers having these heart problems.
This fits perfectly with the 3 women with ejection fraction decline and 2 out of 9 women with heart scarring having reduced heart function.
More research and care need to be addressed for this symptomatic subgroup of female �鶹�� carriers.

Comment on An annual physical brings a sigh of relief to this Duchenne MD caregiver by Betty Vertin

Betty Vertin — Tue, 07 Jul 2026 22:18:24 +0000

In reply to Mary Amsbaugh. Thank you for reading my column and for your kind words. I hope your grandson loves band!

Comment on FDA review begins for full approval bids on 2 Duchenne therapies by Asim Diab

Asim Diab — Tue, 07 Jul 2026 03:54:33 +0000

Please update me about FDA approval for the treatment of LGMD 2i

Comment on FDA review begins for full approval bids on 2 Duchenne therapies by Pushpalatha

Pushpalatha — Sat, 04 Jul 2026 05:44:41 +0000

My son muscular dystopia 15 years

Comment on The search for better accommodations for my disease progression continues by Robin Carlino

Robin Carlino — Fri, 03 Jul 2026 20:48:57 +0000

Oh Rob,
Your articles always touch me and this one leads me to prayer. May you be blessed to find the help you need and be able to take care of your needs! May your next cup of coffee truly be a self-made blessing! xo+

Comment on An annual physical brings a sigh of relief to this Duchenne MD caregiver by Mary Amsbaugh

Mary Amsbaugh — Thu, 02 Jul 2026 21:34:15 +0000

Dear Betty,
I’ve been reading your letters for around six years and have wanted to thank you for sharing. When our grandson was diagnosed at four and we joined this terrible club, we couldn’t imagine what came next. No one can possibly imagine their children or themselves in this world. I don’t shy away from the subject but don’t invite many people into our world either. You are so honest about the day to day but also show us how normal it can become. Our Isaac turns eleven next week as he returns to Cincinnati for his bi-annual check up. Of course he has issues with the affects of the disease and medications but he is a “normal “ boy who has friends, plays the piano and loves legos. He looks forward to fifth grade because he can join band. All the hopes and dreams are still there. Your articles show that your family moves forward no matter what.

Comment on FDA review begins for full approval bids on 2 Duchenne therapies by Corrado

Corrado — Thu, 02 Jul 2026 14:37:06 +0000

Good news but what patients are involved?

Comment on �鶹�� says DOJ memo threatens community care rights by Veila Locke

Veila Locke — Tue, 30 Jun 2026 15:19:52 +0000

As a former caregiver to my son who was diagnosed with muscular dystrophy.
At home care is absolutely essential to the well being and quality of life for those living with disabilities. Nursing homes are not cost effective so why is the Federal. Government trying to intervene in what should be up to the States?

Comment on �鶹�� says DOJ memo threatens community care rights by Samantha Bahri

Samantha Bahri — Mon, 29 Jun 2026 22:04:28 +0000

Hello,
Could you please put together a letter that we can send to our state representatives?
I have seen that done before for research funding. Maybe the �鶹�� could put some type of letter together and send it out to all of us and we can sign and send it to our representatives. Just an idea.

Comment on RGX-202 gene therapy meets main goal in Phase 3 �鶹�� clinical trial by Bradley Sweeting

Bradley Sweeting — Mon, 29 Jun 2026 18:51:49 +0000

Hello, my family is located in Orlando FL we are very interested in this gene therapy for our son who is 4. We are seeking approval for Elevidys but it seems controversial. Any o e able to give some feedback?